Gene Therapy

FDA Green-Lights Roche Spinal Muscular Atrophy Drug, First Oral Therapy

FDA Green-Lights Roche Spinal Muscular Atrophy Drug, First Oral Therapy

2 days ago   |   Xconomy

The FDA on Friday approved a new spinal muscular atrophy drug that patients can take at home. Risdiplam is a liquid medicine intended for daily use that was developed by Roche...
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Production of Modified Vaccinia Ankara Virus by Intensified Cell Cultures: A Comparison of Platform Technologies for Viral Vector Production

3 days ago   |   Wiley

Abstract Modified Vaccinia Ankara virus is a promising vector for vaccination against various challenging pathogens or the treatment of some types of cancers. Because this...
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PhD student studies MS gene therapy treatments

4 days ago   |   Genetics Institute


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FDA Approves First Cell-Based Gene Therapy For Adult Patients with Relapsed or Refractory MCL

5 days ago   |   Gene Therapy

Posted on: 4 August 2020, The U.S. Food and Drug Administration approved Tecartus , a cell-based gene therapy for treatment of adult patients diagnosed with mantle cell...
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AbbVie Walks From Voyager R&D Pact Spanning Alzheimer's, Parkinson's

AbbVie Walks From Voyager R&D Pact Spanning Alzheimer's, Parkinson's

6 days ago   |   Xconomy   |   2 articles

A partnership between Voyager Therapeutics and AbbVie developing gene therapies for Alzheimer's and Parkinson's has ended without a drug for either disease reaching human...
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AbbVie cans Voyager Alzheimer's, Parkinson's gene therapy pacts

6 days ago   |   Fierce Biotech   |   2 articles

AbbVie cans Voyager Alzheimer's, Parkinson's gene therapy pacts ntaylor Tue, 08/04/2020 - 06:10
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New understanding of CRISPR-Cas9 tool could improve gene editing

11 days ago   |   Phys

Within a mere eight years, CRISPR-Cas9 has become the go-to genome editor for both basic research and gene therapy. But CRISPR-Cas9 also has spawned other potentially powerful...
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Researchers develop new cytosine base editors with high specificity and precision

14 days ago   |   Phys   |   2 articles

Base editors, which enable production of highly efficient targeted point mutations in genomic DNA without causing double-stranded DNA breaks, hold great promise for gene...
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FDA demands more data from Solid Bio to lift gene therapy hold

14 days ago   |   Fierce Biotech   |   2 articles

FDA demands more data from Solid Bio to lift gene therapy hold ntaylor Mon, 07/27/2020 - 08:02
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AveXis Inc.: Research and Development Professionals - Gene Therapy

16 days ago   |   San Diego Biotechnology   |   2 articles

AveXis Inc.: OverviewWe're Growing and looking for talented Research professionals!Ready to join a team committed to moving gene therapies into the clinical and co San Diego...
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World Biotechnology Congress 2019

Hilaris Conferences is going to host its premier World Biotechnology Congress 2019 during October 01-02, 2019, Valencia, Spain. Biotechnology 2019 Congress aim to create a... Read more ...

World Biotechnology Congress 2019

Hilaris Conferences is going to host its premier World Biotechnology Congress 2019 during October 01-02, 2019, Valencia, Spain. Biotechnology 2019 Congress aim to create a... Read more ...

2nd International Conference on Tissue Science and Regenerative Medicine

This conference is designed for experts in academia and industries working in the tissue science and regenerative field, this conference will examine cutting-edge research in... Read more ...

Scientists Say: Expect More Rainfall Variability for California

Scientists Say: Expect More Rainfall Variability for California

A new study by researchers from the Climate and Ecosystem Sciences Division at Berkeley Lab has shown that a tropical weather pattern will bring a 50% increase in winter... Read more ...

Berkeley Lab Founder Ernest Lawrence to Be Honored With Memorial Highway in...

Berkeley Lab Founder Ernest Lawrence to Be Honored With Memorial Highway in South Dakota

Ernest Lawrence in Canton, South Dakota, in 1913. Lawrence attended Canton High School and received a bachelor's degree in chemistry from the University of South Dakota in 1922... Read more ...

Seres Sets Sights on FDA After C. Diff Microbiome Therapy Scores in Phase 3

Seres Sets Sights on FDA After C. Diff Microbiome Therapy Scores in Phase 3

An experimental Seres Therapeutics capsule of live bacteria has met the goals of a pivotal study evaluating it as a treatment for a type of recurrent gut infection, preliminary... Read more ...

New research reveals previously hidden features of plant genomes

An international team led by the Plant Phenotyping and Imaging Research Centre at the University of Saskatchewan and researchers at Agriculture and Agri-Food Canada has decoded... Read more ...

Third breakthrough demonstrates photosynthetic hacks can boost yield...

Plants are factories that manufacture yield from light and carbon dioxide-but parts of this complex process, called photosynthesis, are hindered by a lack of raw materials and... Read more ...

New tools in the fight against lethal citrus disease

Scientists are closer to gaining the upper hand on a disease that has wiped out citrus orchards across the globe. New models of the bacterium linked to the disease reveal... Read more ...

De novo synthesis of a wide range of nucleoside analogs using simple achiral...

A team of researchers from Simon Fraser University and Merck & Co. has developed a de novo synthesis technique for creating a wide range of nucleoside analogs using simple... Read more ...

Creative block of molecular evolution: Adaptive mutations repeat themselves...

A group of scientists from Skoltech and the Institute for Information Transmission Problems of RAS showed, using Lake Baikal amphipods as an example, that parallel evolution... Read more ...

Puradigm, LLC announces successful tests of its proactive air and surface...

Results from a study done by the University of Florida using the SARS-CoV-2 virus show a significant decrease in infectivity of the virus immediately after exposure to... Read more ...

Imaging method highlights new role for cellular “skeleton” protein

LA JOLLA-While your skeleton helps your body to move, fine skeleton-like filaments within your cells likewise help cellular structures to move. Now, Salk researchers have... Read more ...